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CelluTarget
·
Multifocal Motor Neuropathy
· Clinical Trials
Phase 2
Recruiting
NCT06254482
Votoplam (PTC518)
Sponsored by
PTC Therapeutics ↗
View on ClinicalTrials.gov ↗
Timeline
Study Dates
Start Date
January 2024
Est. Completion
December 2029
Enrollment Target
90 participants
Status
Recruiting
Study Design
Primary Endpoint
Long-term safety and tolerability of extended PTC518 dosing in participants who completed the initial PIVOT-HD trial
Registry
ClinicalTrials.gov Record
Registry ID
NCT06254482
Direct Link
clinicaltrials.gov/NCT06254482 ↗
Related Treatment
Treatment Being Studied
Votoplam (PTC518) →