Phase 2
Recruiting
NCT06254482

Votoplam (PTC518)

View on ClinicalTrials.gov ↗
Timeline
Study Dates
Start Date
January 2024
Est. Completion
December 2029
Enrollment Target
90 participants
Status
Recruiting
Study Design
Primary Endpoint
Long-term safety and tolerability of extended PTC518 dosing in participants who completed the initial PIVOT-HD trial
Registry
ClinicalTrials.gov Record
Registry ID
NCT06254482
Related Treatment
Treatment Being Studied
Votoplam (PTC518)